Genetics: Gene Therapy
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Marine-Based Therapies for Cancer by atcg » Wed, 01/03/2007 - 01:42 |
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by Jamie_Cruikshank Mon, 03/07/2016 - 12:23 |
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RNA approaches for treatment of SMA in human motor neurons by Jon Moulton » Wed, 07/01/2015 - 18:22 |
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by Jon Moulton Wed, 07/01/2015 - 18:22 |
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Eteplirsen, Morpholino to Treat DMD; 168 Week Data: 6MWT, PFT, and Safety by Jon Moulton » Tue, 04/28/2015 - 21:00 |
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by Jon Moulton Tue, 04/28/2015 - 21:00 |
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Exon skipping approach to duchenne muscular dystrophy by Jon Moulton » Fri, 02/13/2015 - 21:08 |
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by Jon Moulton Fri, 02/13/2015 - 21:08 |
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Long-term 10-oligo cocktail in mice for muscular dystrophy by Jon Moulton » Wed, 02/04/2015 - 16:41 |
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by Jon Moulton Wed, 02/04/2015 - 16:41 |
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Pompe Disease: Block making Glycogen Synthase 1 for Substrate Reduction by Jon Moulton » Wed, 10/29/2014 - 15:50 |
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by Jon Moulton Wed, 10/29/2014 - 15:50 |
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Antisense Morpholino oligo starts phase III trial by Jon Moulton » Thu, 10/02/2014 - 16:05 |
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by Jon Moulton Thu, 10/02/2014 - 16:05 |
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Blocking intronic poly-A signal restores full-length expression by Jon Moulton » Tue, 08/19/2014 - 15:13 |
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by Jon Moulton Tue, 08/19/2014 - 15:13 |
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Morpholinos suppress mutant huntingtin expression & attenuate neurotoxicity by Jon Moulton » Mon, 07/07/2014 - 18:23 |
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by Jon Moulton Mon, 07/07/2014 - 18:23 |
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PPMO restores dystrophin, won't halt disease in late stage dko mice by Jon Moulton » Thu, 06/19/2014 - 20:48 |
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by Jon Moulton Thu, 06/19/2014 - 20:48 |
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Morpholino to Intronic Repressor Element1 in SMA Mouse Models by Jon Moulton » Tue, 04/29/2014 - 15:54 |
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by Jon Moulton Tue, 04/29/2014 - 15:54 |
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Dystrophin repair, mdx mice: new muscle-homing peptide-morpholino conjugate by Jon Moulton » Wed, 04/16/2014 - 15:52 |
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by Jon Moulton Wed, 04/16/2014 - 15:52 |
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Antisense Oligo-Based Therapy in Human Erythropoietic Protoporphyria by Jon Moulton » Tue, 04/01/2014 - 16:37 |
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by Jon Moulton Tue, 04/01/2014 - 16:37 |
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What Can We Learn From Clinical Trials of Exon Skipping for DMD? by Jon Moulton » Thu, 03/13/2014 - 15:19 |
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by Jon Moulton Thu, 03/13/2014 - 15:19 |
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Parent advocacy of molecular medicine for Duchenne muscular dystrophy by Jon Moulton » Thu, 03/06/2014 - 17:20 |
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by Jon Moulton Thu, 03/06/2014 - 17:20 |
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Electrophysiological Biomarkers in Spinal Muscular Atrophy: Preclinical by Jon Moulton » Tue, 02/11/2014 - 17:10 |
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by Jon Moulton Tue, 02/11/2014 - 17:10 |
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Antisense suppression of donor splice site mutations in dystrophin xcript by Jon Moulton » Thu, 02/06/2014 - 18:52 |
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by Jon Moulton Thu, 02/06/2014 - 18:52 |
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Make or break for first splice-modulating agents by Jon Moulton » Mon, 11/04/2013 - 20:41 |
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by Jon Moulton Mon, 11/04/2013 - 20:41 |
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Context Dependent Effects of Chimeric Peptide Morpholino Conjugates by Jon Moulton » Fri, 09/27/2013 - 17:01 |
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by Jon Moulton Fri, 09/27/2013 - 17:01 |
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Eteplirsen for the treatment of duchenne muscular dystrophy by Jon Moulton » Thu, 08/01/2013 - 11:24 |
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by Jon Moulton Thu, 08/01/2013 - 11:24 |
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Exon skipping for SMN2: Toward a Treatment for SMA by Jon Moulton » Fri, 04/26/2013 - 08:37 |
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by Jon Moulton Fri, 04/26/2013 - 08:37 |
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Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe SMA mice by Jon Moulton » Thu, 01/24/2013 - 11:44 |
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by Jon Moulton Thu, 01/24/2013 - 11:44 |
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Morpholino+Peptide Neutralizes RNA Toxicity in Mouse Myotonic Dystrophy by Jon Moulton » Mon, 01/14/2013 - 12:36 |
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by Jon Moulton Mon, 01/14/2013 - 12:36 |
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Dual Myostatin & Dystrophin Exon Skips by Morpholino + CPP for DMD by Jon Moulton » Wed, 12/19/2012 - 10:45 |
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by Jon Moulton Wed, 12/19/2012 - 10:45 |
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Dantrolene Enhances Antisense Exon Skipping in Human & Mouse Models of DMD by Jon Moulton » Wed, 12/12/2012 - 14:27 |
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by Jon Moulton Wed, 12/12/2012 - 14:27 |
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